Signs of weakness start when the boys are between 3 and 5 years of age (sometimes earlier). At first, the weakness is seen mostly in the legs and hips. The children may:
Eventually this weakness also makes walking more difficult and a wheelchair is needed. Gradually, all the muscles become very weak, including the muscles used for breathing and the heart.
There is a drug available in the US that will be of benefit to Vincent at an annual cost of €441,000 plus shipping costs every 13 weeks. Staff at Temple Street Children’s Hospital has agreed to administer the medication. The family are working hard to get this medication for Vincent and your support is greatly appreciated.
DMD Organ System Involvement
Lets Erase DMD
How DMD Manifests